A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments. A newpaper ...

A Santa Cruz family now has a fully adaptable van for their 12-year-old son, Joaquin, who lives with Duchenne muscular dystrophy, thanks to nearly $100,000 raised by the community and Santa Cruz ...

HUDSON — Like many 20-year-olds, Jake Marrazzo struggles with time management and procrastination. So he figured he'd write a book about it, targeting younger children. "I feel like I've never really ...

12-year-old Deklan Locke, who has Duchenne muscular dystrophy, uses a power wheelchair and raises awareness about the disease. Duchenne muscular dystrophy is a rare genetic disorder that causes muscle ...

EDITOR'S NOTE: This story has been updated to correct that the branch of Highmark that initially denied the request for coverage was Highmark Blue Cross Blue Shield Delaware, not the provider's ...

Early intervention and individualized therapy can help children maintain mobility, build confidence, and participate more fully in daily life. WASHINGTON, DC, UNITED ...

Jamesy Raffone of Manalapan is defying the experts, learning to drive despite Duchenne muscular dystrophy. The man least shocked is his father.

Two Boca Raton brothers with muscular dystrophy received autographed balls from Cristiano Ronaldo and VIP tickets during the ...

Like most mothers, I only saw perfection when my first son was born. That quickly changed when we began to question pediatricians about his physical and cognitive delays. Don’t worry, they said. Boys ...

The Muscular Dystrophy Family Foundation is offering a $2,000 educational scholarship. Applicants must be Indiana residents with muscular dystrophy or a related neuromuscular disease. Applications are ...

Eleven-year-old Charlotte Colella and her mother Alexa Colella pose in front of merchandise available for their fundraiser, set for 6 p.m. Tuesday at downtown Champaign's Fire Doll Studios.

Shares of FibroGen Inc. FGEN fell 23% premarket on Wednesday after the company said its investigational treatment for Duchenne muscular dystrophy failed to meet its primary and secondary endpoints in ...