Current evidence does not support the use of random forest classifiers as standalone screening tools for ATTR-CM.

Patients with FCS who took plozasiran continued to show sustained TG reductions in year 3 of the PALISADE open-label ...

The use of antifibrotics in patients with PPF and IPF is higher and increases faster at academic centers compared with ...

The substantial burden of Gaucher disease (GD) type 3 extends to caregivers and health care systems, as documented in a ...

A psychiatric history may be linked to higher odds of experiencing an NPE in children prescribed montelukast, an add-on ...

Phenotypically defined MDS stem cells with enhanced stemness and self-renewal characteristics identified relapse risk more ...

Patients with Huntington disease (HD) at a site in Colorado became the first US participants dosed with SKY-0515, an RNA ...

Investigators in China have documented the first successful use of nerandomilast in a patient with psoriasis and ILD that ...

GLS is shown to detect clinically meaningful myocardial dysfunction in patients with ATTR-CM, even when ejection fraction ...

In a new study, second-line ruxolitinib was associated with marked regression of splenomegaly and with cytopenias in patients ...

A mother relives the nightmare of her son’s FCS-related death when her daughter, who also has FCS, is hospitalized with acute ...

A 12-week modified yoga program appeared to be associated with improvements in selected patient-reported outcome domains ...